Publication - Abstract
Jul 24, 2018
RNA Biology
K.H. Asrani, L. Cheng, C.J. Cheng and R.R. Subramanian
Arginase I (ARG1) deficiency is an autosomal recessive urea cycle disorder, caused by deficiency of the enzyme Arginase I, resulting in accumulation of arginine in blood. Current Standard of Care (SOC) for ARG1 deficiency in patients or those having detrimental mutations of ARG1 ...
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Publication - Summary
Apr 12, 2019
Journal of Controlled Release
S. Patel, R.C. Ryals, K.K.Weller, M.E. Pennesi and G. Sahay
Gaurav Sahay’s lab at Oregon Health and Science University describe a systematic study of lipid nanoparticles (LNPs) for delivering mRNA to the retina. Eleven formulations were made using NanoAssemblr technology and some were administered by subretinal injection in mice. Th...
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